As of October 6, 2023, Amgen officially acquired Horizon Therapeutics. For our cystinosis community using PROCYSBI as a therapeutic...
read moreThe long awaited Cystinosis Advocate Newsletter is here. Choose from research updates, advocacy efforts, family stories, events, cystinosis support...
read moreIn May 2023, Novartis acquired the investigational autologous hematopoietic stem cell (HSC) gene therapy program for the treatment of...
read moreCelebrate Halloween from home this year. ALAB invites you to a free, online event that will test your spooky...
read moreTest your knowledge of everything Halloween. ALAB members are hosting a free, online trivia night. October 29th at 8:30pm...
read moreOn October 21, 2023, the Advanced Therapies Program will host the 9th Annual WORLDFair. Open to both patients and...
read moreJoin us on and leading up to May 7th to promote cystinosis awareness, education and fundraising efforts. Our 7th...
read moreBy taking part in Rare Disease Day you help provide a greater understanding and acceptance of cystinosis and living...
read moreHealogix Market Research would like to hear from the cystinosis community. If you use *or have used* Cystadrops and...
read moreResearchers, clinicians, industry and advocacy representatives attending CRN Nashville have been invited to exhibit research findings, treatment breakthroughs, and...
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