lysosomal storage disorder

WORLDFair for Lysosomal Conditions

On October 21, 2023, the Advanced Therapies Program will host the 9th Annual WORLDFair. Open to both patients and...

February 28th marks the 12th annual Rare Disease Day (RDD). Observed on the rarest day of the year, the...

The Dicks Family sat down for a candid conversation with Daniel Levine from Global Genes. During the latest podcast,...

We are going virtual! The CRN is introducing a series of virtual meetups taking place this fall. Available to...

AVROBIO has released a brochure providing detail on investigational gene therapies for lysosomal storage disorders. Earlier this year, AVROBIO’s...