In honor of 5th Annual Cystinosis Awareness Day a new global initiative has been announced: the Cystinosis Warrior Impact...
read moreClinical researchers from the Stanford Neuromuscular department are looking for individuals who have been diagnosed with Cystinosis Myopathy, to...
read moreCould newborn screening provide a turning point in the natural history of cystinosis? Review the latest publication “Newborn Screening: Review of...
read moreData from the AVROBIO Phase 1/2 investigational gene therapy for cystinosis was released today at WORLDSymposium in San Diego....
read moreVaincre les Maladies Lysosomales has announced funding for a new research project benefitting the cystinosis community: Characterization of Respiratory...
read moreCystinosis researcher, Ana Francisco and her team at Montefiore Medical Center/Einstein College of Medicine are exploring disease impact on...
read moreAVROBIO is looking for perspectives from the cystinosis community. They will be conducting a small focus group to help...
read moreInterim CRN President, Tim Wyman, has written an open letter to the cystinosis community. You can read it here.
read moreSupport the first annual Miles for Moose fundraiser.
read moreSubscribe today to receive updates on the latest news and events.