Dr. Gahl is the Director of the Undiagnosed Diseases Program, a Senior Investigator in the Medical Genetics Branch and...
read moreThis past winter we lost a revolutionary in the cystinosis world, Dr. Jerry Schneider. During his time at the...
read morePress release originally published May 17, 2022 on Avrobio.com. New early data show key visual motor integration, visual perception...
read moreLeadiant, the makers of Cystaran eye drops, are opening up the floor for a Town Hall Q&A on Wednesday,...
read morePlease click here for the latest updates from Leadiant on the Cystadrops shortage. If you have further questions, please...
read moreAs of today, November 12th, AllianceRx Walgreens Prime is unable to fulfill any orders of CYSTARAN. Leadiant’s full announcement...
read moreIn a statement from Leadient Biosciences on October 9th, the company announced an availability shortage may impact cystinosis patients...
read moreBeginning September 15, 2020, Recordati Rare Diseases announced the availability of CYSTADROPS across the United States. CYSTADROPS are a...
read moreTo address the shortage of Cystaran eye drops some members of our community may have encountered recently, Leadient Biosciences...
read moreRecordati announced approval of an eye drop treatment to reduce corneal crystals. “We are pleased to bring Cystadrops® to...
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