Gene Transfer May Be Preventative But Not Curative for a Lysosomal Transport Disorder

Author: Claire Hippert, Grégor Dubois, Carole Morin, Olivier Disson, Sandy Ibanes, Chantal Jacquet, Reto Schwendener, Corinne Antignac, Eric J Kremer, Vasiliki Kalatzis

Year: 2008

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