2026 CRN Scientific Symposium

Advancing the Future of Cystinosis Care.

The CRN Scientific Symposium brings together physicians, clinicians, researchers, and scientists for a peer-to-peer exploration of emerging developments in cystinosis and lysosomal storage disorders. This one-day meeting will examine advances across the cystinosis research and clinical landscape; from newborn screening and novel approaches to treatment and drug delivery to emerging gene, mRNA, and cell-based therapies. Sessions will also explore advances across the broader lysosomal storage disorder landscape and their potential implications for the future of cystinosis research and therapeutic development. This event will foster exchange, collaboration, and discussion among colleagues working to advance the understanding and treatment of cystinosis.

Symposium Chair

We are honored to announce the symposium will be Chaired by Elizabeth Ames, MD, PhD. She serves as Clinical Assistant Professor at the University of Michigan and is Co-Director at the Michigan NORD Rare Disease Center of Excellence. 

Featured Topics

• • Newborn screening in cystinosis
  • Novel approaches to ocular drug delivery
  • Gene, mRNA, and cell-based therapies
  • Prodrug development
  • Lessons from other lysosomal storage disorders
  • Evolving standards of care and international guidelines

Agenda and speakers are subject to change.

Registration

Your registration includes admission to symposium sessions, networking opportunities, and breakfast/lunch/reception hour as outlined in the agenda.  

Location 

• Weber’s Hotel 3050 Jackson Ave, Ann Arbor, MI 48103
• This is a one-day event. For overnight accommodations, hotel rooms are based on availability. Symposium speakers and board members will reserve rooms via Dana Marshall 

Help Spread the Word 

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For questions, email info@cystinosis.org.