gene therapy

Cystinosis Symposium Announced for Healthcare Professionals

The New York Academy of Medicine is the location for this “first of its kind” event for healthcare professionals...

In May 2023, Novartis acquired the investigational autologous hematopoietic stem cell (HSC) gene therapy program for the treatment of...

Press release originally published May 17, 2022 on Avrobio.com. New early data show key visual motor integration, visual perception...

Data from the AVROBIO Phase 1/2 investigational gene therapy for cystinosis was released today at WORLDSymposium in San Diego....

In a quarterly update, AVROBIO announced: “Data from the patients dosed to date across three indications continue to...

AVROBIO Announces 100% Kidney Substrate Reduction at 12 Months Post-Gene Therapy in...

November 17, 2020 – AVROBIO announced that data suggests functional and clinical improvements for the first cystinosis patient at...

Learn more about gene therapy as it relates to the cystinosis community. Dr. Paul Grimm from from Stanford University...

We are going virtual! The CRN is introducing a series of virtual meetups taking place this fall. Available to...

AVROBIO announces the second patient with cystinosis has been dosed in the company’s AVR-RD-04 investigational gene therapy Phase 1/2...