With the hustle and bustle of the holidays, the new year can certainly sneak up on us. Start 2025 off...
read moreNovartis, the company now leading the investigational stem cell gene therapy trial for cystinosis, has shared a new community...
read moreJoin us as we celebrate the 7th Annual Cystinosis Awareness Day with an electrifying regional meetup, courtesy of the...
read moreThe New York Academy of Medicine is the location for this “first of its kind” event for healthcare professionals...
read moreOn the heels of #WorldKidneyDay we congratulate Dr Roz Mannon on her Medal of Excellence. This is one of...
read moreRecordati Rare Diseases announced the launch of a new educational website: www.cystinosisinfocus.com. The site aims to help families manage...
read moreAmgen has partnered with Believe Limited and the Cystinosis Research Network to bring back the third annual, Speak Up,...
read moreAs of October 6, 2023, Amgen officially acquired Horizon Therapeutics. For our cystinosis community using PROCYSBI as a therapeutic...
read moreThe long awaited Cystinosis Advocate Newsletter is here. Choose from research updates, advocacy efforts, family stories, events, cystinosis support...
read moreIn May 2023, Novartis acquired the investigational autologous hematopoietic stem cell (HSC) gene therapy program for the treatment of...
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