This summer we reached a milestone – over $40,000 in scholarships awarded since our program’s inception. Congratulations to the...
Read moreBy Cystinosis Research Network
September 29, 2021
Members of the CRN’s Scientific Review Board have compiled articles for those interested in learning more about an additional...
Read moreBy Cystinosis Research Network
August 18, 2021
In a quarterly update, AVROBIO announced: “Data from the patients dosed to date across three indications continue to...
Read moreBy Cystinosis Research Network
August 17, 2021
Recordati Rare Diseases announced the launch of a new educational website: www.cystinosisinfocus.com. The site aims to help families manage...
Read moreAmgen has partnered with Believe Limited and the Cystinosis Research Network to bring back the third annual, Speak Up,...
Read moreAs of October 6, 2023, Amgen officially acquired Horizon Therapeutics. For our cystinosis community using PROCYSBI as a therapeutic...
Read moreThe long awaited Cystinosis Advocate Newsletter is here. Choose from research updates, advocacy efforts, family stories, events, cystinosis support...
Read moreIn May 2023, Novartis acquired the investigational autologous hematopoietic stem cell (HSC) gene therapy program for the treatment of...
Read moreCelebrate Halloween from home this year. ALAB invites you to a free, online event that will test your spooky...
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