Partnering with RDMD, this program aims to accelerate cystinosis research to ultimately improve treatment options. We welcome you to...
Read moreBy Cystinosis Research Network
July 9, 2020
We are pleased to announce a collaboration between the Cystinosis Research Network (CRN) and Cystinosis Ireland to fund a...
Read moreBy Cystinosis Research Network
July 8, 2020
AVROBIO announces the second patient with cystinosis has been dosed in the company’s AVR-RD-04 investigational gene therapy Phase 1/2...
Read moreBy Cystinosis Research Network
July 6, 2020
The Neuromuscular Clinic at Massachusetts General Hospital (MGH) led by Dr. Reza Seyedsadjadi, is currently enrolling participants for a...
Read moreEmory University in Atlanta, Georgia, is actively recruiting for the Cohort 0 control groupin the CYStem clinical trial. While...
Read moreA new chapter in cystinosis research has begun. Novartis has officially opened the next phase of its CYStem Phase...
Read moreFor our families using Cystadrops, we received the following information from Recordati. This update was in response to direct...
Read moreNovartis has announced the Phase I/II CYStem clinical trial will recruit children ages 2-5 with nephropathic cystinosis. The trial...
Read moreThe CRN-funded QUALIFY-US study, also known as the Quality of Life study, is wrapping up this month. Our researchers...
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