NoMuRiC (Nonsense Mutation Readthrough in Cystinosis) A Phase II Clinical Trial of ELX-02 for Treatment of Cystinosis (McGill University...
Read moreBy Cystinosis Research Network
August 7, 2019
CIRM Board Approves New Clinical Trial for Rare Childhood Disease Original article published on the CIRM website, June 20,...
Read moreBy Cystinosis Research Network
June 22, 2019
Genetic testing is now being offered to cystinosis families at a discounted rate. However, you may be wondering, who...
Read moreBy Cystinosis Research Network
June 19, 2019
The Neuromuscular Clinic at Massachusetts General Hospital (MGH) led by Dr. Reza Seyedsadjadi, is currently enrolling participants for a...
Read moreEmory University in Atlanta, Georgia, is actively recruiting for the Cohort 0 control groupin the CYStem clinical trial. While...
Read moreA new chapter in cystinosis research has begun. Novartis has officially opened the next phase of its CYStem Phase...
Read moreFor our families using Cystadrops, we received the following information from Recordati. This update was in response to direct...
Read moreNovartis has announced the Phase I/II CYStem clinical trial will recruit children ages 2-5 with nephropathic cystinosis. The trial...
Read moreThe CRN-funded QUALIFY-US study, also known as the Quality of Life study, is wrapping up this month. Our researchers...
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