Cystinosis Ireland and the CRN are delighted to announce they will jointly fund research project entitled “Perturbations in the...
Read moreBy Cystinosis Research Network
February 27, 2021
February 12, 2021Dear Cystinosis Community: We wanted to share an update from Leadiant Biosciences regarding the CYSTARAN® (cysteamine ophthalmic...
Read moreBy Cystinosis Research Network
February 15, 2021
In Honor of Laura’s 35th Birthday and Rare Disease Day. An article by Marybeth Krummenacker I was trying to...
Read moreBy Cystinosis Research Network
February 13, 2021
Recordati Rare Diseases announced the launch of a new educational website: www.cystinosisinfocus.com. The site aims to help families manage...
Read moreAmgen has partnered with Believe Limited and the Cystinosis Research Network to bring back the third annual, Speak Up,...
Read moreAs of October 6, 2023, Amgen officially acquired Horizon Therapeutics. For our cystinosis community using PROCYSBI as a therapeutic...
Read moreThe long awaited Cystinosis Advocate Newsletter is here. Choose from research updates, advocacy efforts, family stories, events, cystinosis support...
Read moreIn May 2023, Novartis acquired the investigational autologous hematopoietic stem cell (HSC) gene therapy program for the treatment of...
Read moreCelebrate Halloween from home this year. ALAB invites you to a free, online event that will test your spooky...
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