In Honor of Laura’s 35th Birthday and Rare Disease Day. An article by Marybeth Krummenacker I was trying to...
Read moreBy Cystinosis Research Network
February 13, 2021
AVROBIO Announces 100% Kidney Substrate Reduction at 12 Months Post-Gene Therapy in...
Read moreBy Cystinosis Research Network
February 9, 2021
Thanks in part to volunteers at both the 2017 and 2019 CRN Family Conferences, this study was able to...
Read moreBy Cystinosis Research Network
January 26, 2021
The next phase of clinical development for the CF10 prodrug to treat cystinosis has been announced. The Cystinosis Foundation...
Read moreThe Neuromuscular Clinic at Massachusetts General Hospital (MGH) led by Dr. Reza Seyedsadjadi, is currently enrolling participants for a...
Read moreEmory University in Atlanta, Georgia, is actively recruiting for the Cohort 0 control groupin the CYStem clinical trial. While...
Read moreA new chapter in cystinosis research has begun. Novartis has officially opened the next phase of its CYStem Phase...
Read moreFor our families using Cystadrops, we received the following information from Recordati. This update was in response to direct...
Read moreNovartis has announced the Phase I/II CYStem clinical trial will recruit children ages 2-5 with nephropathic cystinosis. The trial...
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